1. Ambulatory function in spinal muscular atrophy: Age-related patterns of progression Montes, Jacqueline; McDermott, Michael P.; Mirek, Elizabeth; Mazzone, Elena S.; Main, Marion; Glanzman, Allan M.; Duong, Tina; Young, Sally Dunaway; Salazar, Rachel; Pasternak, Amy; Gee, Richard; de Sanctis, Roberto; Coratti, Giorgia; Forcina, Nicola; Fanelli, Lavinia; Ramsey, Danielle; Milev, Evelin; Civitello, Matthew; Pane, Marika; Pera, Maria Carmela; Scoto, Mariacristina; Day, John W.; Tennekoon, Gihan; Finkel, Richard; Darras, Basil T.; Muntoni, Francesco; De Vivo, Darryl C.; Mercuri, Eugenio 2018 Articles Spinal muscular atrophyAgingWalkingNeurology
2. Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool Ramsey, Danielle; Scoto, Mariacristina; Mayhew, Anna; Main, Marion; Mazzone, Elena S.; Montes, Jacqueline; de Sanctis, Roberto; Salazar, Rachel; Young, Sally Dunaway; Glanzman, Allan M.; Pasternak, Amy; Quigley, Janet; Mirek, Elizabeth; Duong, Tina; Gee, Richard; Civitello, Matthew; Tennekoon, Gihan; Pane, Marika; Pera, Maria Carmela; Bushby, Kate; Day, John; Darras, Basil T.; De Vivo, Darryl C.; Finkel, Richard; Mercuri, Eugenio; Muntoni, Francesco 2017 Articles PsychometricsSpinal muscular atrophyNeurosciencesMedicine